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Supramolecular nanosubstrate-mediated delivery system enables CRISPR-Cas9 knockin of hemoglobin beta gene for hemoglobinopathies

  • Peng Yang
  • , Shih Jie Chou
  • , Jindian Li
  • , Wenqiao Hui
  • , Wenfei Liu
  • , Na Sun
  • , Ryan Y. Zhang
  • , Yazhen Zhu
  • , Ming Long Tsai
  • , Henkie I. Lai
  • , Matthew Smalley
  • , Xinyue Zhang
  • , Jiayuan Chen
  • , Zulema Romero
  • , Dahai Liu
  • , Zunfu Ke
  • , Chang Zou
  • , Chin Fa Lee
  • , Steven J. Jonas
  • , Qian Ban
  • Paul S. Weiss, Donald B. Kohn, Kai Chen, Shih Hwa Chiou, Hsian Rong Tseng*
*此作品的通信作者

研究成果: Article同行評審

36 引文 斯高帕斯(Scopus)

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Biochemistry, Genetics and Molecular Biology