Keyphrases
Potential Therapeutics
100%
Stem Cell-derived
100%
Neuronal Cells
100%
Histone Deacetylase Inhibitor (HDACi)
100%
Induced Pluripotent Stem Cells (iPSCs)
100%
Spinal muscular Atrophy
100%
SMN2
33%
SMN1 Gene
22%
Screening Platform
11%
Clinical Trials
11%
Protein Expression
11%
Biological Activity
11%
Neuromuscular Disease
11%
Autosomal Recessive
11%
Survival Motor Neuron
11%
Non-neuronal Cells
11%
Paralogous Genes
11%
Small Molecule Libraries
11%
Exon 7
11%
Splicing Defect
11%
Cellular Models
11%
Tuj1
11%
Diminished Expression
11%
Therapeutic Development
11%
Neuronal Cell Lines
11%
Inactivating mutation
11%
Medicine and Dentistry
Histone Deacetylase Inhibitor
100%
Spinal Muscular Atrophy
100%
Tetrapeptide
100%
Induced Pluripotent Stem Cell
100%
Survival Motor Neuron Protein
22%
Clinical Trial
11%
Protein Expression
11%
Exon
11%
Neuromuscular Disease
11%
Autosomal Recessive Inheritance
11%
Non-Neuronal Cell
11%
Cellular Model
11%
Neuronal Cell Line
11%
Splicing Defect
11%
Paralogy
11%
Diseases
11%
Biological Activity
11%
Biochemistry, Genetics and Molecular Biology
Histone Deacetylase
100%
Induced Pluripotent Stem Cell
100%
Tetrapeptide
100%
SMN2
60%
Clinical Trial
20%
Exon
20%
Protein Expression
20%
Survival of Motor Neuron
20%
Autosomal Recessive Inheritance
20%
Paralogy
20%
Splicing Defect
20%
Biological Activity
20%
Neuroscience
Stem Cell
100%
Histone Deacetylase Inhibitor
100%
Tetrapeptide
100%
Spinal Muscular Atrophy
100%
Survival Motor Neuron Protein
22%
Cell Line
11%
Protein Expression
11%
Neuromuscular Disorder
11%
Exon
11%
Splicing Defect
11%
Pharmacology, Toxicology and Pharmaceutical Science
Histone Deacetylase Inhibitor
100%
Spinal Muscular Atrophy
100%
Tetrapeptide
100%
Survival Motor Neuron Protein
22%
Clinical Trial
11%
Biological Activity
11%
Neuromuscular Disease
11%
Diseases
11%